Pluripotent stem cell-based drug discovery uncovers sildenafil as a treatment for mitochondrial disease

Annika Zink, DaoFu Dai, Annika Wittich, Marie-Thérèse Henke, Giulia Pedrotti, Sonja Heiduschka, Guillem S. Aguilar, Tancredi Massimo Pentimalli, Christian Brueser, Sofia Notopoulou, Aleksandra Zhaivoron, Abdul Rahim Umar, Laura Petersilie, Caleb Jerred, Jesper Bergmans, Fabian Schumacher, Jan Keller-Findeisen, Agnieszka Rybak-Wolf, Daniel Stach, Jeanette Reinshagen, Andrea Zaliani, Undine Haferkamp, Liliya Euro, Alessia Di Donfrancesco, Chiara Santanatoglia, Enrica Cappellozza, Marta Suarez Cubero, Mario Pavez-Giani, Oleh Bakumenko, David Meierhofer, Alan Foley, Susanne Morales-Gonzalez, Isabella Tolle, Diran Herebian, Daniele Bonesso, Ildiko Szabo, Giulia Cecchetto, Sakurako Wong, Monica Moresco, Alessandra Maresca, Ilaria Decimo, Merel J.W. Adjobo-Hermans, Burkhard Kleuser, Lukas Cyganek, Chris Mühlhausen, Lars Schlotawa, Valeria Tiranti, Andrea Rossi, Ertan Mayatepek, Chiara La Morgia, Valerio Carelli, Thomas Klopstock, Felix Distelmaier, Ghanim Ullah, Stefan Jakobs, Nikolaus Rajewsky, Christine R. Rose, Spyros Petrakis, Frank Edenhofer, Werner Koopmann, Dario Brunetti, Pawel Lisowski, Anu Suomalainen, Antonio del Sol, Emanuela Bottani, Ole Pless, Markus Schuelke, Alessandro Prigione. Medrxiv 2025
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Annika Zink, DaoFu Dai, Annika Wittich, Marie-Thérèse Henke, Giulia Pedrotti, Sonja Heiduschka, Guillem S. Aguilar, Tancredi Massimo Pentimalli, Christian Brueser, Sofia Notopoulou, Aleksandra Zhaivoron, Abdul Rahim Umar, Laura Petersilie, Caleb Jerred, Jesper Bergmans, Fabian Schumacher, Jan Keller-Findeisen, Agnieszka Rybak-Wolf, Daniel Stach, Jeanette Reinshagen, Andrea Zaliani, Undine Haferkamp, Liliya Euro, Alessia Di Donfrancesco, Chiara Santanatoglia, Enrica Cappellozza, Marta Suarez Cubero, Mario Pavez-Giani, Oleh Bakumenko, David Meierhofer, Alan Foley, Susanne Morales-Gonzalez, Isabella Tolle, Diran Herebian, Daniele Bonesso, Ildiko Szabo, Giulia Cecchetto, Sakurako Wong, Monica Moresco, Alessandra Maresca, Ilaria Decimo, Merel J.W. Adjobo-Hermans, Burkhard Kleuser, Lukas Cyganek, Chris Mühlhausen, Lars Schlotawa, Valeria Tiranti, Andrea Rossi, Ertan Mayatepek, Chiara La Morgia, Valerio Carelli, Thomas Klopstock, Felix Distelmaier, Ghanim Ullah, Stefan Jakobs, Nikolaus Rajewsky, Christine R. Rose, Spyros Petrakis, Frank Edenhofer, Werner Koopmann, Dario Brunetti, Pawel Lisowski, Anu Suomalainen, Antonio del Sol, Emanuela Bottani, Ole Pless, Markus Schuelke, Alessandro Prigione. Medrxiv 2025