Transabdominal ultrasound guided AAV9-GFP delivery in fetal pigs: a translational and minimally invasive model for in utero fetal gene therapy.

Di Donfrancesco A, Adelizzi A, Giri A, Duchi R, Boito S, Barandalla M, Massaro G, Santanatoglia C, Cappellozza E, Perota A, Di Meo I, Tiranti V, Bottani E, Galli C, Persico N, Brunetti D.Gene Ther. 2025